AIRNA Therapeutics soon will test its novel RNA editing approach in patients for the first time, starting with the rare genetic disease alpha-1 antitrypsin deficiency (AATD), but the company is eyeing conditions impacting large populations as well, including cardiometabolic diseases. It will take AIR-001 for AATD into the clinic while also building out its RNA editing platform and R&D pipeline with $155m in series B venture capital funding announced on 1 April.
AIRNA To Take RNA Editing Into The Clinic With $155m Series B Round
Previously Raised $90m In Series A Cash
CEO Kris Elverum told Scrip about the start-up’s platform for editing RNA to correct genetic variants that cause harm and to reproduce healthy variants as a means of treating disease.

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CEO Kris Elverum told Scrip about the start-up’s platform for editing RNA to correct genetic variants that cause harm and to reproduce healthy variants as a means of treating disease.
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