Fueled By Connections: Making It Happen In Rare Disease

Agios’s Sarah Gheuens talks to In Vivo about the responsibility of providing new therapies to rare disease populations, building trust with historically underserved communities, and why she loves working with small molecules.  

Rare
It is estimated that 3000 to 8000 have PK Deficiency in the US and Five EU Major Markets • Source: Shutterstock

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