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Lessons From Europe: Orphan Drug Valuations Show Limits Of Cost Effectiveness

 
• By Cathy Kelly

Biogen, Sanofi executives says US should learn from experience of European health technology assessment bodies as Institute for Clinical and Economic Review embarks on initiative to adapt its value framework to orphan drugs.

The European experience with conducting health technology assessments demonstrates the limitations of current approaches to comparative effectiveness, according to Biogen Inc. VP EU+ Market Access and Pricing Chris Leibman.

That could inform the way US payers approach valuing orphan drugs for reimbursement decisions, Leibman suggested at the Institute for Clinical and Economic Review stakeholder meeting on orphan drug pricing...

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