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How To Conduct A Multi-Company Trial For Rare Pediatric Diseases

 
• By Brenda Sandburg

US FDA draft guidance suggests efficacy endpoints for testing multiple drug products in the same clinical trials; advances an FDA-EMA joint proposal promoting innovative approaches for development of Gaucher disease medicines.

children's soft toy teddy bear with pills takes the temperature of a mercury glass thermometer. child' disease.

The US FDA is casting a spotlight on a new approach to the development of drugs for rare pediatric diseases in which companies would test multiple product candidates in the same clinical trial.

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