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US FDA May Create Rare Disease Expert Pool For Advisory Committee Reviews

 
• By Derrick Gingery

FDA's Peter Stein calls idea "useful"; rare disease experts would temporarily serve on standing advisory committees when needed. 

FDA Advisory Committee Feature image

The US FDA may create a pool of rare disease specialists to enhance advisory committee expertise when relevant applications are under review.

Agency officials have yet to finalize a plan, but in theory would develop a list of experts that could be used as temporary members of an advisory committee when needed

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