Karyopharm’s Selinexor: US FDA Unconvinced By Efficacy In Single-Arm Trial

Oncologic Drugs Advisory Committee will consider whether approval for Karyopharm’s proposed refractory myeloma therapy selinexor should await results from an ongoing Phase III randomized trial.

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Will a single arm be enough for Karyopharm’s proposed refractory myeloma therapy selinexor?

The US FDA appears to have significant reservations about the clinical profile of Karyopharm’s selinexor heading into a Feb. 26 review of the proposed treatment for relapsed refractory multiple myeloma.

The NDA filing is based on a single-arm Phase II study (STORM) in fourth-line multiple myeloma, in which selinexor 80 mg twice-weekly was administered in conjunction with dexamethasone 20 mg. In the trial, “the combination of selinexor and dexamethasone demonstrated limited efficacy and significant toxicity in patients with RRMM,” FDA says in its pre-meeting

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