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InnoSkel Targets Rapid UK Patient Access For Gene Therapy

INS-101 Is Intended For Rare Bone Disorder

 
• By Ian Schofield

The number of “innovation passports” handed out by the UK Medicines and Healthcare products Regulatory Agency is growing as more companies seek to take advantage of the tools and flexibilities available under the ILAP. InnoSkel is one such company.

genetic rare disease Wilson disease
Gene therapy could be used to treat a rare bone disorder • Source: Alamy

French biotech InnoSkel says that close collaboration with the authorities and accelerated patient access were the key reasons why it decided to apply for an “innovation passport” under the UK’s Innovative Licensing and Access Pathway (ILAP). The passport was awarded this week to INS-101, a first-in-class gene therapy intended to treat the rare bone disorder, spondyloepiphyseal dysplasia congenita (SEDc).

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More from Europe

Switzerland Simplifies Imports Of Unauthorized Drugs To Tackle Drug Shortages

 
• By Eliza Slawther

Swiss authorities have introduced temporary measures that will make it easier for health care professionals to import medicines that are either not authorized or not available in Switzerland, which will particularly benefit pediatric drugs, in light of ongoing shortages.

EU ‘Can’t Expect Industry To Give Up Proprietary Insights’ Under Health Data & Clinical Trials Regulations

 
• By Eliza Slawther

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Raising Drug Prices In The EU Could Take Years, Even If Pharma Effort Succeeds

 
• By Cathy Kelly

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Non-Submissions To UK HTA Body Could Increase Unless Commercial Environment Improves, Warns Industry

 
• By Leela Barham

Finding ways to lower the rebates paid by the pharmaceutical industry to the UK government and fostering partnerships to make the UK a more attractive launch market could help reduce the number of terminated technology appraisals conducted by NICE, the health technology appraisal institute, says the UK pharmaceutical industry.

More from Geography

Switzerland Simplifies Imports Of Unauthorized Drugs To Tackle Drug Shortages

 
• By Eliza Slawther

Swiss authorities have introduced temporary measures that will make it easier for health care professionals to import medicines that are either not authorized or not available in Switzerland, which will particularly benefit pediatric drugs, in light of ongoing shortages.

EU ‘Can’t Expect Industry To Give Up Proprietary Insights’ Under Health Data & Clinical Trials Regulations

 
• By Eliza Slawther

Both the EU Clinical Trials Regulation and the European Health Data Space Regulation have the potential to improve harmonization and be highly valuable for industry – but the importance of protecting company data will be paramount, a life sciences consultant says.

How Tumult At US FDA Could Impact Merger and Acquisition Strategy

 
• By Joseph Haas and Nielsen Hobbs

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