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Gene Therapy For Lethal Glycogen Storage Disease Wins EMA PRIME Designation

Ten products have been granted PRIME designation so far this year

 
• By Neena Brizmohun

Investigational products from Ultragenyx and MinervaX secured a place on the European Medicines Agency’s priority medicines scheme this month.

PRIME can help fast track the development of drugs for unmet medical needs • Source: Alamy

DTX401, a one-time gene therapy for glycogen storage disease type Ia (GSDIa), and GBS-NN/NN2, a maternal vaccine for preventing group B streptococcal infection in newborns, are the latest investigational products to make it onto the European Medicines Agency’s PRIME (priority medicines) scheme.

DTX401 and GBS-NN/NN2, which are being developed by Ultragenyx Pharmaceutical and MinervaX respectively, were accepted onto the scheme by the EMA this month –

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