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Hemophilia Gene Therapy Hemgenix Gets Funding In England, With More Talks Underway In Europe

 
• By Ian Schofield

After an initial funding rejection last year, CSL Behring’s gene therapy for hemophilia B is to be made available to English patients under the Innovative Medicines Fund via a “first-of-its-kind” agreement. Hemgenix is also the subject of a funding deal in Denmark.

Blood gene therapy
The UK and Denmark have agreed funding for a gene therapy for hemophilia • Source: Shutterstock

CSL Behring says its gene therapy for hemophilia B, Hemgenix (etranacogene dezaparvovec), will be made available in England immediately and hopes the first patient will be treated by the autumn, after the health technology assessment body NICE said the therapy should be reimbursed through a managed access scheme under the Innovative Medicines Fund.

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