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Raptor rises on US Procysbi OK

 
• By Donna Young

Raptor Pharmaceuticals gained the US FDA's OK on 30 April to market Procysbi (cysteamine bitartrate) as a therapy for adults and children as young as six years to manage nephropathic cystinosis, a rare, life-threatening metabolic lysosomal storage disorder that causes toxic accumulation of cystine in all cells, tissues, and organs in the body.

Raptor Pharmaceuticals gained the US FDA's OK on 30 April to market Procysbi (cysteamine bitartrate) as a therapy for adults and children as young as six years to manage nephropathic cystinosis, a rare, life-threatening metabolic lysosomal storage disorder that causes toxic accumulation of cystine in all cells, tissues, and organs in the body.

The approval triggered a 17% rise in Raptor's shares on 30 April, before the stock closed at $6.90, a gain...

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