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PTC wins conditional EU Translarna approval

 
• By Gemma Collier

PTC Therapeutics has been granted conditional approval from the European Commission for its Duchenne muscular dystrophy (DMD) drug Translarna (ataluren), which has yet to produce Phase III data.

PTC Therapeutics has been granted conditional approval from the European Commission for its Duchenne muscular dystrophy (DMD) drug Translarna (ataluren), which has yet to produce Phase III data.

Translarna has been approved to treat nonsense mutation Duchenne muscular dystrophy in 28 EU countries, as well as Iceland, Liechtenstein and Norway. The drug is the first to work by...

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