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Spark's Gene Therapy Is On The Cusp Of Approval; Now It Gets Interesting

 
• By Jessica Merrill

Spark's Luxturna is all but guaranteed to reach the US market as the first gene therapy following a unanimous positive FDA advisory committee review. Discussions about cost and value are sure to intensify.

Eye

Spark Therapeutics Inc. put together a convincing lineup of patients and advocates to provide testimony urging FDA's Cellular, Tissue and Gene Therapies Advisory Committee to support US FDA approval of Luxturna (voretigene neparvovec) for a rare inherited blindness.

The testimony at the panel's Oct

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