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Luxturna Approved In EU: Novartis Outlines Lessons For Gene Therapy Strategies

 
• By Francesca Bruce

The European Commission has officially approved Luxturna, Novartis/Spark Therapeutics’ transformative gene therapy. The Swiss firm tells Scrip how the lessons it expects to learn from launching its first gene therapy will inform its future strategy in this new field.

Dart
Luxturna wins marketing appoval in the EU

The European Commission has officially approved Luxturna (voretigene neparvovec), Novartis AG’s one-time gene therapy for inherited retinal dystrophy caused by RPE65 gene mutations.

This is the company’s first move into gene therapy and the approval is something of a landmark for Novartis. What...

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