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Phase II Success Positions Ra For Potential Blockbuster Opportunity In Myasthenia Gravis

 
• By Joseph Haas

Ra hopes to launch a Phase III program for zilucoplan next year, with a goal of bringing an alternative therapy for MG patients into competition with Alexion’s Soliris.

Medic staff at work in the laboratory. Background

Ra Pharmaceuticals Inc.’s successful top-line Phase IIb data with complement 5 (C5) inhibitor zilucoplan in generalized myasthenia gravis (gMG), unveiled on Dec. 10, gives the biotech an opportunity toward blockbuster sales with a self-administered therapy that offers several points of differentiation compared to Alexion Pharmaceuticals Inc.’s Soliris (eculizumab).

One of the highest-priced drugs in the world, Soliris became the only drug approved specifically to treat myasthenia gravis (MG)...

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Actuate Is Looking For A Buyer To Advance Pancreatic Cancer Candidate

 
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• By Andrew McConaghie

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