Retrophin Bolsters Portfolio With Orphan Technologies Buyout

The rare disease-focused firm will pay $90m up front to acquire Orphan Technologies and its Phase I/II enzyme replacement therapy for homocystinuria. Earnouts up to $427m are possible as well.

Black Swan Event (face masks). Concept. A rare and unexpected event that has a major effect, such as a financial crash or pandemic. It is a metaphor often used in science or economics.
Deal adds to Retrophin's rare diseases pipeline

Retrophin, Inc. is turning to business development to build its rare disease-focused pipeline about a year after a Phase III failure threw its plans into disarray – the biotech has agreed to pay $90m up front with significant earnout potential to acquire privately held Orphan Technologies Ltd. and its enzyme replacement therapy candidate for homocystinuria (HCU).

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