Vertex Pharmaceuticals Incorporated has taken another step to expand beyond its market-leading cystic fibrosis (CF) franchise by linking up with Skyhawk Therapeutics, Inc. and its RNA-splicing technology.
The companies have been fairly coy about the details, simply stating that that their alliance is aimed at "the discovery and development of novel small molecules that modulate RNA splicing for the treatment of serious diseases," using Skyhawk's SkySTAR platform