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Pharming And Orchard Seek Stem Cell Solution To Hereditary Angioedema

Duo To Develop Hematopoietic Stem Cell Gene Therapy

 
• By Sten Stovall

Orchard Therapeutics of the US and Dutch biotech Pharming have agreed to jointly research, develop, manufacture and commercialize the former’s newly disclosed investigational ex vivo autologous hematopoietic stem cell gene therapy as a treatment for hereditary angioedema.

Stem Cell Gene Therapy
Companies hope to ultimately find a gene therapy cure for HAE • Source: Alamy

Netherlands-basedPharming Group N.V. is tapping the gene therapy abilities of Orchard Therapeutics Limited of the US in hopes of developing a therapy that could ultimately cure hereditary angioedema (HAE), but their development plans are in the early stages.

Orchard is a gene therapy specialist whose approach harnesses the power of genetically modified blood stem cells and seeks to correct the

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