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Stock Watch: Not So Fast, Gene Editors

Ground-breaking Phase I Results For Gene Editing Light An Early Fuse

 
• By Andy Smith

Intellia’s announcement of the first in vitro gene editing proof of principle sent shockwaves through the life science investment space. But are there still many known unknowns.

Stock Watch Image, Andy Smith
ANDY SMITH OFFERS A LIFE SCIENCE INVESTOR'S PERSPECTIVE ON BIOPHARMA BUSINESS

In a week when the merger of a neutron star and a black hole was reported to have disrupted the very fabric of space-time, the announcement of the first results of a successful in vivo gene editing study in humans elicited a seismic stock market shift back here on Earth. In contrast with cosmic events that occur millions of light years away, the time and risks from interim Phase I results to commercialization are prone to underestimation.

The recent conference presentation and journal publication of the first human data in six patients with hereditary transthyretin amyloidosis with...

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Draig Is All Fired Up To Transform Neuropsychiatric Field

 
• By Kevin Grogan

Wales-based group launches with $140m series A.

BIO Notebook: Policy Problems, ACIP’s Future, BI Is Popular, Makary On FDA-Industry Ties

 
• By Sarah Karlin-Smith and Mandy Jackson

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Lilly Agrees To Acquire PCSK9 Base-Editing Partner Verve

 
• By Joseph Haas

Instead of opting in on Phase II-ready PCSK9-targeted VERVE-102, Lilly will buy its partner for up to $1.3bn. Analysts call the deal a bargain for Lilly, but fair to Verve.