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Amicus Spins Out Rare Disease Gene Therapy Pipeline, Raises $200m

 
• By Joseph Haas

While Amicus will transfer the gene therapy portfolio’s R&D risk to Caritas, it retains a financial interest in many of the spinout’s programs. Pompe candidate AT-GAA accepted for FDA review.

Empty dirt road which splits in two, concept for life choices or decisions
Amicus will split out its gene therapy R&D into Caritas

Amicus Therapeutics, Inc. is spinning out its rare disease gene therapy portfolio into a separate publicly traded company and using the increasingly popular special purpose acquisition corporation (SPAC) model to do so. The Philadelphia-area biotech announced the deal, a separate financing and acceptance of a US regulatory filing for its combination product for Pompe disease during an investor call on 29 September.

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