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Amicus Spins Out Rare Disease Gene Therapy Pipeline, Raises $200m

 
• By Joseph Haas

While Amicus will transfer the gene therapy portfolio’s R&D risk to Caritas, it retains a financial interest in many of the spinout’s programs. Pompe candidate AT-GAA accepted for FDA review.

Empty dirt road which splits in two, concept for life choices or decisions
Amicus will split out its gene therapy R&D into Caritas

Amicus Therapeutics, Inc. is spinning out its rare disease gene therapy portfolio into a separate publicly traded company and using the increasingly popular special purpose acquisition corporation (SPAC) model to do so. The Philadelphia-area biotech announced the deal, a separate financing and acceptance of a US regulatory filing for its combination product for Pompe disease during an investor call on 29 September.

In the fourth Arya Sciences SPAC transaction managed by Perceptive Advisors, the gene therapy pipeline compiled by Amicus via its 2018 buyout of Celenex and a subsequent collaboration with researchers at the University of Pennsylvania will become a standalone company called Caritas Therapeutics

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