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Marinus, With Ztalmy Approval, Takes First Step Into Seizure Disorder Market

 
• By Jessica Merrill

The company will launch Ztalmy for an ultra-rare pediatric seizure disorder but hopes to expand to larger indications in the future. CEO Scott Braunstein talks to Scrip about the launch.

start line
Marinus has reached its commercial start • Source: Alamy

Marinus Pharmaceuticals, Inc. has secured its first US Food and Drug Administration approval, and it is for Ztalmy (ganaxolone) for a rare pediatric seizure disorder, coming after a long development road and several failed clinical trials. The company announced the FDA approval of Ztalmy, an oral suspension, on 18 March for the treatment of seizures associated with cyclin-dependent kinase-like 5 deficiency disorder (CDD) in patients two years of age and older.

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