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‘Substantial’ Discount Helps Zolgensma Win Access In UK

 
• By Francesca Bruce

The English and Scottish health technology appraisal bodies NICE and the Scottish Medicines Consortium have given the green light to Novartis/Avexis’ costly gene therapy, Zolgensma.

Morning in Jebel Shams, Oman
NHS England 'moved mountains' to strike Zolgensma deal • Source: Shutterstock

Novartis AG/Avexis’ Zolgensma (onasemnogene abeparvovec) is to be reimbursed on the National Health Service in both England and Scotland.

In England the product will be fast tracked to patients on the back of “evidence of exceptional benefit” before final...

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More from Geography

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• By Lisa Takagi

While the government announces eight to 15% cuts to the four products, industry groups urges for its operational improvement without expansion.

Precigen’s Papzimeous Approval Allows US FDA CBER Director To Emphasize Flexibility

 
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