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EMA Says Yes To PRIME Designations For Wet AMD & HAE Gene Therapies

 
• By Neena Brizmohun

Two gene therapies, from Molecular Therapeutics and Intellia Therapeutics respectively, are among the four new products the European Medicines Agency accepted onto it priority medicines scheme this month.

gene and color background
Two new gene therapy candidates have won PRIME designation • Source: Shutterstock

NTLA-2002 and 4D-150, which are single-dose, gene therapy candidates for hereditary angioedema and neovascular age-related macular degeneration (wet AMD) respectively, are among the latest products to be accepted onto PRIME, the European Medicines Agency’s priority medicines scheme for drugs for unmet medical needs.

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