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Orphan Drugs Dominate Latest EU Filings

 
• By Neena Brizmohun

Sotatercept, marstacimab, elafibranor, eplontersen, mirvetuximab soravtansine, troriluzole and tiratricol are among the latest products that the European Medicines Agency has started reviewing for potential EU marketing approval.

A new batch of drugs are under review in the EU • Source: Shutterstock

Seven orphan drugs including MSD’s sotatercept, for pulmonary arterial hypertension (PAH), and Pfizer's marstacimab, for patients with hemophilia, are among the latest products that have been filed for review by the European Medicines Agency for potential pan-EU marketing authorization.

Sotatercept is an investigational activin signaling inhibitor that, if approved, “would be the first in its class, bringing a novel approach to address a rare and progressive disease of the...

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