Novartis Takes Huntington's Path With SMA Therapy Branaplam

Priority Has Shifted After Rival Roche's Success

With Roche's oral spinal muscular atrophy therapy Evrysdi off to a strong start after its recent US launch, Novartis is switching its priorities for rival RNA-splicing drug branaplam and putting it into a Phase IIb trial for Huntington's disease.

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Huntington's is a progressive brain disorder caused by a defective gene • Source: Shutterstock

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