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Inozyme Targets Underserved Mineralization Disorders Market With First-In-Class Enzyme Therapy

 
• By Ayisha Sharma

Emerging Company Profile: Fresh from a $73m follow-on offering last year, the US biotech is readying its lead asset for a pivotal trial in ultra-rare but debilitating mineralization disorders that affect infants and children.  

Emerging Company Profile: Inozyme Pharma
ENPP1 Deficiency Can Cause Arterial Calcification And Eventual Death • Source: Shutterstock

Inozyme Pharma Inc. is on a mission to treat two ultra-rare and often fatal mineralization disorders that currently have no approved options with its lead enzyme therapy asset that has the potential to be a ‘pipeline in a product.’

The Boston, MA-headquartered had a strong start with a $50m seed funding in January 2017 followed by a second private round two years later that raised $67m. In July 2020,...

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