Inozyme Targets Underserved Mineralization Disorders Market With First-In-Class Enzyme Therapy

Emerging Company Profile: Fresh from a $73m follow-on offering last year, the US biotech is readying its lead asset for a pivotal trial in ultra-rare but debilitating mineralization disorders that affect infants and children.  

Emerging Company Profile: Inozyme Pharma
ENPP1 Deficiency Can Cause Arterial Calcification And Eventual Death • Source: Shutterstock

Inozyme Pharma Inc. is on a mission to treat two ultra-rare and often fatal mineralization disorders that currently have no approved options with its lead enzyme therapy asset that has the potential to be a ‘pipeline in a product.’

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