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Mirum’s Rare Disease Strategy: A Blueprint For Sustainable Growth

 
• By David Wild

From a $7m discarded asset to a $336m commercial portfolio, In Vivo looks inside Mirum Pharma’s disciplined strategy for identifying, acquiring and revitalizing overlooked rare disease programs while building toward billion-dollar potential.

(Shutterstock)
Key Takeaways
  • In transforming a $7m discarded asset into a $336m commercial portfolio, Mirum has demonstrated the value of overlooked programs that don't meet portfolio criteria at larger companies.
  • The company is utilizing a capital-efficient model to strive for faster returns than traditional biotech approaches.
  • Strategic pipeline expansion into adjacent therapeutic areas, such Mirum's move into Fragile X, could maximize operational efficiency while creating new billion-dollar opportunities.

At its core, Mirum Pharma is a business

CEO Chris Peetz sat down with In Vivo to discuss Mirum’s commercial momentum, near-term catalysts and the company’s

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