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Shire's Elaprase Follow-On's Future Uncertain After Trial Miss

 
• By Joseph Haas

Specialty pharma says it will continue examining the full dataset for idursulfase formulation intended for pediatric Hunter syndrome patients with cognitive impairment.

woman in a laboratory microscope with microscope slide in hand.toned image.

Executives at Shire PLC speak often of the firm's strong emphasis on rare diseases, but one of its pipeline candidates for Hunter syndrome faces an unclear future after missing both the primary and key secondary endpoint in Phase II/III study.

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