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Spark's Gene Therapy Hemophilia Data Give Investors The Jitters

 
• By Emily Hayes

Company explains how it will design upcoming Phase III hemophilia A study of SPK-8011 for success, but some analysts still think it's risky business.

Piggy coin bank and stock candlestick chart going down for investments and savings loss

Spark Therapeutics Inc. is moving its SPK-8011 gene therapy into a Phase III hemophilia study soon, despite disappointing Phase I/II data and concerns about competition from BioMarin Pharmaceutical Inc.'s BMN 270.

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