BioMarin Says It's Got The Hemophilia Therapy Data For Approval And Value

 
• By Jessica Merrill

The company will begin discussions with regulators in the US and Europe for a gene therapy for hemophilia A based on the results of new data, with a launch targeted for late 2020. Durability remains a question.

Red blood cells. Blood elements - red blood cells responsible for oxygen carrying over, regulation pH blood, a food and protection of cages of an organism. - Illustration

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