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Novartis Close To EU Approval For Zolgensma At Last

SMA Drug Backed by CHMP

 
• By Alexandra Shimmings

Novartis’s AveXis unit has received a CHMP nod for the spinal muscular atrophy gene therapy at its latest meeting, sending it on the final steps to market in the EU.    

Genmanipulation
Zolgensma is a closely-watched gene therapy • Source: Shutterstock

After several delays plus a row over a controversial lottery-style managed access program in Europe, Novartis AG’s gene therapy Zolgensma has finally been granted a positive opinion by the EU’s CHMP.

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