What looked like increasing momentum for Larimar Therapeutics, Inc.’s program to develop the first drug therapy for Friedrich’s ataxia was dashed at least temporarily on 25 May, as the company announced a US Food and Drug Administration clinical hold due to deaths in a non-human primate toxicology study. The news came two weeks after the release of Phase I clinical data the company said showed proof-of-concept and days after it announced a $95m follow-on financing – which is now on hold as well.
Clinical Hold Halts Larimar’s Friedrich’s Ataxia Candidate And Financing
Looking to develop the first drug therapy for FA, Larimar gets US FDA hold due to deaths in non-human primate study. This alters clinical development timelines and fundraising plans for the firm.
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