Krystal Biotech, Inc. believes it is positioned to deliver the first genetically corrective treatment to patients with the rare and debilitating genetic skin disease dystrophic epidermolysis bullosa (DEB), following a successful Phase III study testing its topical gene therapy Vyjuvek (beremagene geperpavec, B-VEC), showing a benefit on wound healing compared to placebo.
Krystal Sees Success With Topical Gene Therapy In Debilitating Rare Skin Disorder
A regulatory filing for Vyjuvek in the US is targeted for the first half of 2022 following the positive results of a Phase III trial, positioning Krystal for its first commercial launch.
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