The cautionary tale of Orphazyme A/S, which enjoyed a sky-high share price based on social media chatter before its lead candidate arimoclomol fell foul of US regulators a year ago, has reached a sorry conclusion with the Danish biotech being sold off to KemPharm, Inc. for peanuts.
Orphazyme’s Sorry Story Ends In Fire Sale
KemPharm Acquires Assets For Paltry Sum
While Orphazyme's attempts to get approval for arimoclomol failed miserably, new owner KemPharm is confident it can get the oral heat shock protein amplifier across the regulatory finishing line for Niemann-Pick disease type C.
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