Scholar Rock Looks To Augment Existing Therapies In Spinal Muscular Atrophy

 
• By Joseph Haas

Phase III study under way may lead to filing of drug meant to address muscular component of the rare disease, with existing therapies such as Spinraza targeting neurological aspects.

Muscle atrophy
Scholar Rock's approach to SMA focuses on the muscle-function aspects of the disorder • Source: Shutterstock

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