Travere Looks Ahead To Phase III In Homocystinuria

Opportunity Bolstered By Competitor’s Recent HCU Failure

The latest data from a Phase I/II study shows that pegtibatinase can yield a rapid, sustained reduction in homocysteine, the protein behind the underlying cause of the rare disease.

Diet
HCU patients are hoping for a therapy that can loosen dietary restrictions • Source: Shutterstock

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