Agios Pharmaceuticals will take the spotlight at the upcoming European Hematology Association congress with impressive Phase III data expected for Pyrukynd (mitapivat) in non-transfusion dependent alpha- or beta-thalassemia (NTDT).
EHA Preview: Agios Takes Spotlight In Thalassemia
The company expects to have data from transfusion-dependent and non-transfusion dependent patients this year, with a potential expanded US approval in 2025 for Pyrukynd.

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RemeGen is planning to complete enrolment in the global Phase III RemeMG study with telitacicept in generalized myasthenia gravis by the end of 2025 or early 2026. The Chinese firm has already sidelined two other global Phase III trials with the molecule to prioritize the indication.
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