EHA Preview: Agios Takes Spotlight In Thalassemia

The company expects to have data from transfusion-dependent and non-transfusion dependent patients this year, with a potential expanded US approval in 2025 for Pyrukynd.

IFEMA Madrid
The European Hematology Association congress will take place in Madrid, Spain, 13-16 June. • Source: Shutterstock

Agios Pharmaceuticals will take the spotlight at the upcoming European Hematology Association congress with impressive Phase III data expected for Pyrukynd (mitapivat) in non-transfusion dependent alpha- or beta-thalassemia (NTDT).

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