Pfizer Inc. appears closer to launching a gene therapy for hemophilia A, based on the positive results of the Phase III AFFINE study testing giroctocogene fitelparvovec for the treatment of moderately severe to severe hemophilia A versus prophylaxis.
Pfizer’s Hemophilia A Gene Therapy Superior To Prophylaxis In Phase III
The company’s giroctocogene fitelparvovec, partnered with Sangamo, could compete with BioMarin’s hemophilia A gene therapy Roctavian, but longer-term data may be needed.
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