Manufacturers Eye Challenges Of Broadening Cell And Gene Therapy Access

Potential Expansion From Academia To Community

With more advanced therapies gaining approval, companies at ARM’s Cell and Gene Meeting on the Mesa considered hurdles to making their products more broadly available and developing them for larger indications.

3d rendering of Human cell or Embryonic stem cell microscope background
Cell and gene therapy makers are looking beyond rare disease indications • Source: Shutterstock

With a growing number of complex cell and gene therapies approved globally, mostly for rare disease populations, manufacturers are looking at how to make these products more accessible by delivering available treatments through a greater number of health care centers and by developing new treatments for larger patient populations.

Key Takeaways
  • Cell and gene therapy developers want to bring their products to more patients via health care providers closer to home and larger indications.

  • However, community health care providers have limited resources to provide the specialized treatment administration and safety monitoring that cell and gene therapies provide

Launches for approved cell and gene therapies to treat rare diseases and small oncology indications at a limited number of authorized or qualified treatment centers (ATCs or QTCs) – usually academic institutions, transplant centers or regional facilities that have clinical trial experience with these products – have been difficult, to say the least

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