Zevra Seals PRV Sale And Banks $150m

Having picked up Niemann-Pick disease type C drug Miplyffa for a song, the US rare disease specialist is singing all the way to the bank after selling the priority review voucher that came with its approval.

one lone Zebra standing in a field.
Zevra is Greek for zebra, the official symbol of rare disease (Shutterstock)

When Zevra Therapeutics, then known as KemPharm, bought arimoclomol for peanuts with its acquisition of Orphazyme in 2022, it looked like a great bit of business and further confirmation has come with the multi-million dollar sale of a priority review voucher (PRV) linked to the drug.

The US firm got hold of a rare pediatric disease PRV as a result of

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