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Gene Editing Deal Broadens Vertex's CF Base, Doubles CRISPR's Cash

 
• By Mandy Jackson

Vertex Pharmaceuticals made a big financial commitment to expand its cystic fibrosis portfolio beyond drugs for patients with specific genetic mutations to gene-editing therapies that may cure CF via a new partnership with CRISPR Therapeutics that more than doubles the startup firm's cash balance.

Vertex Pharmaceuticals made a big financial commitment to expand its cystic fibrosis portfolio beyond drugs for patients with specific genetic mutations to gene-editing therapies that may cure CF via a new partnership with CRISPR Therapeutics that more than doubles the startup firm's cash balance.

Boston-based Vertex will pay $105m up front, including a $30m equity investment in CRISPR, to develop therapies based on clustered,...

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