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Scrip Asks… What Will Happen In Orphan Drug Pricing In The Next Five Years?

 
• By Scrip Team

Feb 28 is Rare Disease Day. To mark the occasion, Scrip asked experts the question: Do you see orphan drug pricing coming under pressure over the next five years?

Wrench and coins
Are orphan drugs facing greater pricing pressures? • Source: Shutterstock

The orphan drugs business is seen as one with high margins, high entry barriers and limited competitive pressure. But as the field matures, will those dynamics change? To mark Rare Disease Day on Feb. 28, Scrip asked experts the question: Do you see orphan drug pricing coming under pressure over the next five years?

We received a broad range of answers from an equally broad range of stakeholders – from the grandfather of orphan drug companies, Genzyme Corp., to newcomers such as Akari Therapeutics PLC and MyoKardia Inc

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