Hemophilia: How To Please Payers And Secure Market Share

Pharma companies are bringing forward innovative products that are set to shake up the hemophilia market – but convincing payers that they have substantial benefits over the current standards of care will be a challenge. Real-world data and early conversations with payers will be key, new research has found.

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The hemophilia market is expecting an influx of new products currently at the later stages of clinical development, including gene therapies, that will pile pressure on payers looking to contain costs. To secure market access, it will be critical for companies with entirely novel hemophilia therapies, as well as those providing incremental treatment benefits, to start conversations with payers as soon as possible. Care should also be taken over the design of clinical trials in order to maximize a new product's attractiveness.

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