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Chiesi Committed To Becoming A Major Player In Rare Diseases

 
• By Kevin Grogan

The Italian group has got the green light in Europe for Lamzede, the first disease-modifying therapy for alpha mannosidosis and believes the drug, along with Procysbi and an investigational Fabry disease being developed with Protalix, constitute a strong portfolio in the rare metabolic disease area.

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Chiesi is focusing on rare diseases • Source: Shutterstock

Chiesi Farmaceutici SPA's aim of becoming a force in the rare disease space has received a boost with the European Commission granting marketing authorization for Lamzede (velmanase alfa), the first disease-modifying therapy for alpha mannosidosis (AM).

The green light for Lamzede has been given under “exceptional circumstances,” a mechanism to assess treatments of extremely rare disorders...

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