1. Scrip

Scrip's Guide To Spinal Muscular Atrophy Therapies

 
• By Eleanor Malone and Alexandra Shimmings

INFOGRAPHIC: The prospects for patients with spinal muscular atrophy, the leading cause of genetic death in infants, have  been revolutionized by the arrival of the first approved drug for the disease, Biogen’s blockbuster Spinraza. Now, other firms with equally revolutionary product candidates are giving chase. Scrip takes a look at the main contenders.

Editor's note: The table in this Infographic was updated on March 5, 2019, to correct the development stage of Novartis's branaplam to Phase II, not Phase III as previously stated, and on March 8, 2019, to update the corresponding Likelihood of Approval score from 62% to 24%.

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