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Solid Biosciences’ DMD Gene Therapy Undermined By Safety Wobbles

 
• By Alexandra Shimmings

Another setback for the novel therapy leaves rivals Sarepta and Pfizer in a stronger position in a potentially highly rewarding market.

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Not so Solid Ground for the DMD therapy • Source: Shutterstock

Solid Biosciences Inc. has been hit by potential safety issues with its lead gene therapy for Duchenne muscular dystrophy, SGT-001, as it increased the dose in its Phase I/II IGNITE DMD clinical trial. The development sent its shares southwards and could prove a boon to the prospects for

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