BioMarin’s Momentum Grows With Twin Blockbuster Plans
Dwarfism Drug Data Look Promising
The frontrunner in hemophilia A gene therapy has been hit by data doubts, but this and achondroplasia drug could deliver in 2020.
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The frontrunner in hemophilia A gene therapy has been hit by data doubts, but this and achondroplasia drug could deliver in 2020.