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BioMarin’s Momentum Grows With Twin Blockbuster Plans

Dwarfism Drug Data Look Promising

 
• By Andrew McConaghie

The frontrunner in hemophilia A gene therapy has been hit by data doubts, but this and achondroplasia drug could deliver in 2020.

Biomarin
• Source: BioMarin

BioMarin Pharmaceutical Inc. is preparing to bring two first-in-class medicines to market in 2020 and has just provided extra reassurances that the therapies will make a real difference to patients, and help it reach a new growth phase.

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Bristol’s Opdivo + Yervoy Gets FDA Liver, Colorectal Cancer Nods

 
• By Joseph Haas

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Novartis $23bn US Investment Is Music To Trump’s Ears

 
• By Kevin Grogan

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