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BioMarin’s Momentum Grows With Twin Blockbuster Plans

Dwarfism Drug Data Look Promising

 
• By Andrew McConaghie

The frontrunner in hemophilia A gene therapy has been hit by data doubts, but this and achondroplasia drug could deliver in 2020.

Biomarin
• Source: BioMarin

BioMarin Pharmaceutical Inc. is preparing to bring two first-in-class medicines to market in 2020 and has just provided extra reassurances that the therapies will make a real difference to patients, and help it reach a new growth phase.

Chief executive Jean-Jacques Bienaimé and his leadership team visited New York on 14 November to present their commercial vision and...

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