Sarepta Sinks On Mixed DMD Gene Therapy Study

Blames 'Bad Luck In Randomization Process'

Any time advantage Sarepta's Duchenne muscular dystrophy gene therapy may have had over rivals, notably Pfizer, has disappeared after SRP-9001 failed to significantly improve muscle function in a closely watched trial.

dmd
Dystrophin is the protein missing in children born with DMD • Source: Shutterstock

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