Alnylam is recognized as a pioneer of the RNA interference (RNAi) gene-silencing field, but so far it has not been able to produce an out-and-out blockbuster from its innovative platform, instead having to fight it out in a competitive and niche ATTR amyloidosis market with drugs such as OnPattro (patisiran).
In Alnylam’s Search For A Mass-Market Treatment, A Twice Yearly Blood Pressure Injection Could Fit The Bill
Crucial Phase II Readouts This Year
Alnylam is using its RNA interference technology to target hypertension, which could create a true mass-market cardiovascular blockbuster drug for the firm – but upcoming Phase II data will need to be compelling.
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